Halted March 2021 — exploratory analyses suggested potential harm from non-allele-specific HTT lowering. Reframed the field around earlier intervention + allele-selective targeting.

Details

nct_id
NCT03761849
phase
phase_3
status
terminated
domain
huntingtons
indication
Manifest Huntington's Disease
intervention
Tominersen (antisense oligonucleotide targeting HTT)
sponsor
Roche
n_enrolled
791
primary_endpoint
cUHDRS at 101 weeks
Raw fields (1)
metadata
{}

Voting as anonymous. Sign in to attribute your signals.

tokens

Discussion

Posting anonymously. Sign in for attribution.

No comments yet — be the first.