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Spinal Muscular Atrophy ([spinal-muscular-atrophy](/diseases/spinal-muscular-atrophy))[@fda]. Approved by the U.S. Food
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Spinal Muscular Atrophy (SMA) [spinal-muscular-atrophy](/diseases/spinal-muscular-atrophy) is caused
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spinal-muscular-atrophy | spinal-cord - tdp-43 | tdp-43-proteinopathy
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Spinal Muscular Atrophy Background ### Disease Pathophysiology [spinal-muscular-atrophy](/diseases/spinal-muscular-atrophy
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spinal-muscular-atrophy](/diseases/spinal-muscular-atrophy) (SMA). It delivers a functional copy
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spinal-muscular-atrophy (2022)( (2022)](https://doi.org/10.1007/s00115-021-01256-0) 6. [Unknown
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spinal-muscular-atrophy](/diseases/spinal-muscular-atrophy). ## Prognosis NIID is a slowly progressive
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spinal-muscular-atrophy](/diseases/spinal-muscular-atrophy) models, STMN2 expression is reduced, and restoring
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spinal-muscular-atrophy SMN2 exon 7 inclusion batten-disease CLN gene
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spinal-muscular-atrophy](/diseases/spinal-muscular-atrophy), demonstrating broad applicability of ASO technology
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